Abbreviations: AA – Aplastic Anaemia; AL- Acute Leukemia; ALCL- Anaplastic large cell lymphoma; ALL- Acute lymphoblastic leukemia; AML -Acute Myeloid Leukemia; BD- Benign Disorder; BMF- Bone marrow failure; CGD- Chronic granulomatous disease; CLL- Chronic lymphocytic leukemia; CML- Chronic Myeloid Leukemia; CMML- Chronic myelomonocytic leukemia; EB- Epidermolysis bullosa; FA- Fanconi Anemia; JMML- Juvenile myelomonocytic leukemia; SAA- Severe Aplastic Anaemia; CGD- Chronic granulomatous disease; HM- Hematologic malignancies; HL- Hodgkin lymphoma; HP- Hemoglobinopathies; IMD- Inherited metabolic disorders; L- Leukemia; LY- Lymphoma; MDS- Myelodysplastic Syndrome; MF- Myelofibrosis; MM- Multiple Myeloma; NHL- Non-Hodgkin lymphoma; OS- Osteopetrosis; PCD-Plasma Cell Disorder; PID- Primary immune deficiencies; PNH- Paroxysmal nocturnal hemoglobinuria; TM- Thalassemia Major.
a Other diagnoses includes Hemophagocytic lymphohistiocytosis, Wiskott–Aldrich syndrome, Adrenoleukodystrophy and Krabbe disease.
b F-araA PK was evaluated only in 169 patients