Abbreviations: AA –
Aplastic Anaemia; AL- Acute Leukemia; ALCL- Anaplastic large cell
lymphoma; ALL- Acute lymphoblastic leukemia; AML -Acute Myeloid
Leukemia; BD- Benign Disorder; BMF- Bone marrow failure; CGD- Chronic
granulomatous disease; CLL- Chronic lymphocytic leukemia; CML- Chronic
Myeloid Leukemia; CMML- Chronic myelomonocytic leukemia; EB-
Epidermolysis bullosa; FA- Fanconi Anemia; JMML- Juvenile myelomonocytic
leukemia; SAA- Severe Aplastic Anaemia; CGD- Chronic granulomatous
disease; HM- Hematologic malignancies; HL- Hodgkin lymphoma; HP-
Hemoglobinopathies; IMD- Inherited metabolic disorders; L- Leukemia; LY-
Lymphoma; MDS- Myelodysplastic Syndrome; MF- Myelofibrosis; MM- Multiple
Myeloma; NHL- Non-Hodgkin lymphoma; OS- Osteopetrosis; PCD-Plasma Cell
Disorder; PID- Primary immune deficiencies; PNH- Paroxysmal nocturnal
hemoglobinuria; TM- Thalassemia Major.
a Other diagnoses includes Hemophagocytic
lymphohistiocytosis, Wiskott–Aldrich syndrome, Adrenoleukodystrophy and
Krabbe disease.
b F-araA PK was evaluated only in 169 patients